Deep in your muscles, an enzyme called AMPD1 helps turn chemical fuel into usable energy. When it does not work well, muscles tire faster.
Mitochondrial diseases are severe, often untreatable, and they leave human cells unable to grow normally without outside help. A new study published in Nature Metabolism now shows that a single gene ...
UniQure (NASDAQ:QURE) is one of the most promising low-cost stocks to buy now. On February 6, UniQure reported positive updated data from its Phase I/IIa trial of AMT-191, which is a gene therapy for ...
AMT-191 has been granted both Orphan Drug and Fast Track designation by the U.S. Food and Drug Administration.